Long-term effectiveness of enzyme replacement therapy in children with Gaucher disease: results from the NCS-LSD cohort study.

2.50
Hdl Handle:
http://hdl.handle.net/11287/617986
Title:
Long-term effectiveness of enzyme replacement therapy in children with Gaucher disease: results from the NCS-LSD cohort study.
Authors:
Anderson, L. J.; Henley, W. E.; Wyatt, K. M.; Nikolaou, V.; Waldek, S.; Hughes, D. A.; Pastores, G. M.; Logan, Stuart
Abstract:
To determine the effectiveness of enzyme replacement therapies (ERT) for children with Gaucher disease (GD).
Citation:
Long-term effectiveness of enzyme replacement therapy in children with Gaucher disease: results from the NCS-LSD cohort study. 2014, 37 (6):961-8 J. Inherit. Metab. Dis.
Publisher:
Springer
Journal:
Journal of inherited metabolic disease
Issue Date:
Nov-2014
URI:
http://hdl.handle.net/11287/617986
DOI:
10.1007/s10545-014-9693-8
PubMed ID:
24638276
Additional Links:
http://dx.doi.org/10.1007/s10545-014-9693-8
Type:
Journal Article; Multicenter Study; Observational Study; Research Support, Non-U.S. Gov't
Language:
en
ISSN:
1573-2665
Appears in Collections:
2014 RD&E publications; Paediatrics

Full metadata record

DC FieldValue Language
dc.contributor.authorAnderson, L. J.en
dc.contributor.authorHenley, W. E.en
dc.contributor.authorWyatt, K. M.en
dc.contributor.authorNikolaou, V.en
dc.contributor.authorWaldek, S.en
dc.contributor.authorHughes, D. A.en
dc.contributor.authorPastores, G. M.en
dc.contributor.authorLogan, Stuarten
dc.date.accessioned2016-08-05T13:45:34Z-
dc.date.available2016-08-05T13:45:34Z-
dc.date.issued2014-11-
dc.identifier.citationLong-term effectiveness of enzyme replacement therapy in children with Gaucher disease: results from the NCS-LSD cohort study. 2014, 37 (6):961-8 J. Inherit. Metab. Dis.en
dc.identifier.issn1573-2665-
dc.identifier.pmid24638276-
dc.identifier.doi10.1007/s10545-014-9693-8-
dc.identifier.urihttp://hdl.handle.net/11287/617986-
dc.description.abstractTo determine the effectiveness of enzyme replacement therapies (ERT) for children with Gaucher disease (GD).en
dc.language.isoenen
dc.publisherSpringeren
dc.relation.urlhttp://dx.doi.org/10.1007/s10545-014-9693-8en
dc.rightsArchived with thanks to Journal of inherited metabolic diseaseen
dc.subjectWessex Classification Subject Headings::Oncology. Pathology.::Geneticsen
dc.subjectWessex Classification Subject Headings::Paediatricsen
dc.titleLong-term effectiveness of enzyme replacement therapy in children with Gaucher disease: results from the NCS-LSD cohort study.en
dc.typeJournal Articleen
dc.typeMulticenter Studyen
dc.typeObservational Studyen
dc.typeResearch Support, Non-U.S. Gov'ten
dc.identifier.journalJournal of inherited metabolic diseaseen
dc.type.versionPublisheden

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